Search for Clinical Trial Results
Mitochondrial Diseases - 27 Studies Found
Status | Study |
Terminated |
Study Name: RG2133 (2',3',5'-Tri-O-Acetyluridine) in Mitochondrial Disease Condition: Mitochondrial Diseases Date: 2003-05-07 Interventions: Drug: RG2133 (2',3',5'-tri-O-acetyluridine) |
Recruiting |
Study Name: An Observational Study of Patients With Primary Mitochondrial Disease (SPIMM-300) Condition: Primary Mitochondrial Disease Date: 2017-02-03 |
Active, not recruiting |
Study Name: A Study to Evaluate the Safety, Tolerability, and Efficacy of Subcutaneous Injections of Elamipretide (MTP-131) in Subjects With Genetically Confirmed Mitochondrial Disease Previously Treated in the Stealth BioTherapeutics SPIMM-201 Study Condition: Primary Mitochondrial Disease Date: 2016-06-13 Interventions:
|
Completed |
Study Name: Energy Requirements in Mitochondrial Disease Condition:
Date: 2013-01-17 |
Completed |
Study Name: DINAMITE Study Nutritional State and Effect Diet in Mitochondrial Disease Condition: Mitochondrial Disorders Date: 2014-10-31 Interventions: Behavioral: diet intervention The dietary intervention implies optimizing the diet based on individually |
Completed |
Study Name: Open-Label, Dose-Escalating Study Assessing Safety, Tolerability, Efficacy, of RP103 in Mitochondrial Disease Condition: Inherited Mitochondrial Disease, Including Leigh Syndrome Date: 2013-12-17 Interventions: Drug: Cysteamine Bitartrate Cysteamine Bitartrate Delayed-release Capsules |
Recruiting |
Study Name: GDF-15 as a Biomarker for Mitochondrial Disease Condition:
Date: 2010-06-02 Interventions: Procedure: gastric emptying scan subjects will eat a solid |
Recruiting |
Study Name: North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC) Condition:
|
Active, not recruiting |
Study Name: EPI-743 for Mitochondrial Respiratory Chain Diseases Condition: Mitochondrial Diseases Date: 2011-06-07 Interventions: Drug: EPI-743 EPI-743 is administered as a dose escalation from 50 mg bid to 100 mg tid |